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Phase 3 Trial of Crinecerfont in Pediatric Congenital Adrenal Hyperplasia

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In this phase 3 trial, crinecerfont was superior to placebo in reducing elevated androstenedione levels and lowering glucocorticoid doses in pediatric participants with classic congenital adrenal hyperplasia.

​   The New England Journal of Medicine: Search Results in Pediatrics

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